Golodirsen
| Clinical data | |
|---|---|
| Trade names | Vyondys 53 |
| Other names | SRP-4053 |
| AHFS/Drugs.com | Monograph |
| License data |
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| Routes of administration | Intravenous |
| Drug class | Antisense oligonucleotide |
| ATC code | |
| Legal status | |
| Legal status |
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| Identifiers | |
| CAS Number | |
| DrugBank | |
| UNII | |
| KEGG | |
| Chemical and physical data | |
| Formula | C305H481N138O112P25 |
| Molar mass | 8647.401 g·mol−1 |
Golodirsen, sold under the brand name Vyondys 53, is a medication used for the treatment of Duchenne muscular dystrophy. It is an antisense oligonucleotide medication of phosphorodiamidate morpholino oligomer (PMO) chemistry.
The most common side effects include headache, fever, fall, cough, vomiting, abdominal pain, cold symptoms (nasopharyngitis) and nausea.